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WebSep 2, 2024 · “With the creation of Novartis Gene Therapies, we will continue to advance our gene therapy pipeline for rare genetic diseases, to accelerate the delivery of transformative innovation in areas of high unmet need, and to reimagine medicine for patients all around the world.” Webdescribes using a gene’s own DNA sequence to stop its’ functioning, a process that researchers call gene silencing. Originally restricted to biomedical research, gene silencing can now be used therapeutically.13 Phase 3 trials showed that inclisiran was able to lower LDL levels by an average of 54.1% after about business names registration act 2011 austlii
Germany Cell and Gene Therapy Market Focused Insights
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